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CBFB-MYH11 fusion transcripts distinguish acute myeloid leukemias with distinct molecular landscapes and outcomes
Outcomes of acute lymphoblastic leukemia with KMT2A (MLL) rearrangement: the MD Anderson experience
Long term follow-up of a phase II study of cladribine with concurrent rituximab with hairy cell leukemia variant
Treatment-free remission in patients with chronic myeloid leukemia: recommendations of the LALNET expert panel
Tisagenlecleucel immunogenicity in relapsed/refractory acute lymphoblastic leukemia and diffuse large B-cell lymphoma
Economic evaluation of regular transfusions for cerebral infarct recurrence in the Silent Cerebral Infarct Transfusion Trial
Efficacy and safety of daratumumab combined with all-trans retinoic acid in relapsed/refractory multiple myeloma
Early detection of WT1 measurable residual disease identifies high-risk patients, independent of transplantation in AML
Integrated safety analysis of umbralisib, a dual PI3Kδ/CK1ε inhibitor, in relapsed/refractory lymphoid malignancies
Humoral immune reconstitution after anti-BCMA CAR T-cell therapy in relapsed/refractory multiple myeloma
Infectious complications of CAR T-cell therapy across novel antigen targets in the first 30 days
Randomized phase 3 ALCANZA study of brentuximab vedotin vs physician’s choice in cutaneous T-cell lymphoma: final data
Early relapse identifies MCL patients with inferior survival after intensive or less intensive frontline therapy
NUDT15 variants confer high incidence of second malignancies in children with acute lymphoblastic leukemia
Association of race and ethnicity with clinical phenotype, genetics, and survival in pediatric acute myeloid leukemia
Predicting mortality from intracranial hemorrhage in patients who undergo allogeneic hematopoietic stem cell transplantation
Impact of cryopreservation and transit times of allogeneic grafts on hematopoietic and immune reconstitution
Anti-CD25 radioimmunotherapy with BEAM autologous hematopoietic cell transplantation conditioning in Hodgkin lymphoma
Issue Archive
December 14 2021
In this Issue
Table of Contents
BLOOD ADVANCES TALK
EXCEPTIONAL CASE REPORT
STIMULUS REPORT
CBFB-MYH11 fusion transcripts distinguish acute myeloid leukemias with distinct molecular landscapes and outcomes
Clinical Trials & Observations
Benjamin J. Huang,Jenny L. Smith,Yi-Cheng Wang,Kassra Taghizadeh,Amanda R. Leonti,Rhonda E. Ries,Yanling Liu,Pandurang Kolekar,Katherine Tarlock,Robert Gerbing,Erin Crowgey,Scott N. Furlan,Timothy I. Shaw,Kohei Hagiwara,Lisa Wei,Todd M. Cooper,Alan S. Gamis,Richard Aplenc,E. Anders Kolb,Jason E. Farrar,Timothy Triche, Jr,Todd A. Alonzo,Xiaotu Ma,Soheil Meshinchi
Clinical impact of NPM1-mutant molecular persistence after chemotherapy for acute myeloid leukemia
Ing S. Tiong,Richard Dillon,Adam Ivey,James A. Kuzich,Nisha Thiagarajah,Kirsty M. Sharplin,Chung Hoow Kok,Aditya Tedjaseputra,James P. Rowland,Carolyn S. Grove,Emad Abro,Jake Shortt,Devendra K. Hiwase,Ashish Bajel,Nicola E. Potter,Matthew L. Smith,Claire J. Hemmaway,Abin Thomas,Amanda F. Gilkes,Nigel H. Russell,Andrew H. Wei
Outcomes of acute lymphoblastic leukemia with KMT2A (MLL) rearrangement: the MD Anderson experience
Clinical Trials & Observations
Guillaume Richard-Carpentier,Hagop M. Kantarjian,Guilin Tang,C. Cameron Yin,Joseph D. Khoury,Ghayas C. Issa,Fadi Haddad,Nitin Jain,Farhad Ravandi,Nicholas J. Short,Courtney D. DiNardo,Koichi Takahashi,Marina Y. Konopleva,Naval G. Daver,Tapan Kadia,Guillermo Garcia-Manero,Rebecca Garris,Susan O’Brien,Elias Jabbour
SYSTEMATIC REVIEW
Bleeding assessment tools in the diagnosis of VWD in adults and children: a systematic review and meta-analysis of test accuracy
Mohamad A. Kalot,Nedaa Husainat,Sammy Tayiem,Abdallah El Alayli,Ahmad B. Dimassi,Osama Diab,Omar Abughanimeh,Bader Madoukh,Aref Qureini,Barbara Ameer,Jorge Di Paola,Jeroen C.J. Eikenboom,Vicky Jacobs-Pratt,Claire McLintock,Robert Montgomery,James S. O’Donnell,Robert Sidonio, Jr.,Romina Brignardello-Petersen,Veronica Flood,Nathan T. Connell,Paula D. James,Reem A. Mustafa
CLINICAL TRIALS AND OBSERVATIONS
Long term follow-up of a phase II study of cladribine with concurrent rituximab with hairy cell leukemia variant
Clinical Trials & Observations
Dai Chihara,Evgeny Arons,Maryalice Stetler-Stevenson,Constance Yuan,Hao-Wei Wang,Hong Zhou,Mark Raffeld,Liqiang Xi,Seth M. Steinberg,Julie Feurtado,Lacey James-Echenique,Chin-Hsien Tai,Keyur P. Patel,Raul C. Braylan,Katherine R. Calvo,Irina Maric,Alina Dulau-Florea,Robert J. Kreitman
Treatment-free remission in patients with chronic myeloid leukemia: recommendations of the LALNET expert panel
Clinical Trials & Observations
Carolina Pavlovsky,Virginia Abello Polo,Katia Pagnano,Ana Ines Varela,Claudia Agudelo,Michele Bianchini,Carla Boquimpani,Renato Centrone,Monica Conchon,Nancy Delgado,Vaneuza Funke,Isabel Giere,Ingrid Luise,Luis Meillon,Beatriz Moiraghi,Juan Ramon Navarro,Lilian Pilleux,Ana Ines Prado,Soledad Undurraga,Jorge Cortes
Tisagenlecleucel immunogenicity in relapsed/refractory acute lymphoblastic leukemia and diffuse large B-cell lymphoma
Clinical Trials & Observations
Karen Thudium Mueller,Stephan A. Grupp,Shannon L. Maude,John E. Levine,Michael A. Pulsipher,Michael W. Boyer,Keith J. August,G. Doug Myers,Constantine S. Tam,Ulrich Jaeger,Stephen Ronan Foley,Peter Borchmann,Stephen J. Schuster,Edmund K. Waller,Rakesh Awasthi,Bernd Potthoff,Andy Warren,Edward R. Waldron,Fraser McBlane,Andrea Chassot-Agostinho,Theodore W. Laetsch
Economic evaluation of regular transfusions for cerebral infarct recurrence in the Silent Cerebral Infarct Transfusion Trial
Clinical Trials & Observations
Efficacy and safety of daratumumab combined with all-trans retinoic acid in relapsed/refractory multiple myeloma
Clinical Trials & Observations
Kristine A. Frerichs,Monique C. Minnema,Mark-David Levin,Annemiek Broijl,Gerard M. J. Bos,Marie José Kersten,Tuna Mutis,Christie P. M. Verkleij,Inger S. Nijhof,Patricia W. C. Maas-Bosman,Saskia K. Klein,Sonja Zweegman,Pieter Sonneveld,Niels W. C. J. van de Donk
Early detection of WT1 measurable residual disease identifies high-risk patients, independent of transplantation in AML
Clinical Trials & Observations
Juliette Lambert,Jerome Lambert,Xavier Thomas,Alice Marceau-Renaut,Jean-Baptiste Micol,Aline Renneville,Emmanuelle Clappier,Sandrine Hayette,Christian Récher,Emmanuel Raffoux,Arnaud Pigneux,Celine Berthon,Christine Terré,Karine Celli-Lebras,Sylvie Castaigne,Nicolas Boissel,Philippe Rousselot,Claude Preudhomme,Hervé Dombret,Nicolas Duployez
Integrated safety analysis of umbralisib, a dual PI3Kδ/CK1ε inhibitor, in relapsed/refractory lymphoid malignancies
Clinical Trials & Observations
Matthew S. Davids,Owen A. O’Connor,Wojciech Jurczak,Felipe Samaniego,Timothy S. Fenske,Pier Luigi Zinzani,Manish R. Patel,Nilanjan Ghosh,Bruce D. Cheson,Enrico Derenzini,Danielle M. Brander,James A. Reeves,Wanda Knopińska-Posłuszny,John N. Allan,Tycel Phillips,Paolo F. Caimi,Ewa Lech-Maranda,John M. Burke,Richy Agajanian,Ruth Pettengell,Lori A. Leslie,Chan Y. Cheah,Gustavo Fonseca,James Essell,Julio C. Chavez,John M. Pagel,Jeff P. Sharman,Yanzhi Hsu,Hari P. Miskin,Peter Sportelli,Michael S. Weiss,Ian W. Flinn
HEALTH SERVICES AND OUTCOMES
ASH Research Collaborative: a real-world data infrastructure to support real-world evidence development and learning healthcare systems in hematology
William A. Wood,Peter Marks,Robert M. Plovnick,Kathleen Hewitt,Donna S. Neuberg,Sam Walters,Brendan K. Dolan,Emily A. Tucker,Charles S. Abrams,Alexis A. Thompson,Kenneth C. Anderson,Paul Kluetz,Ann Farrell,Donna Rivera,Matthew Gertzog,Gregory Pappas
HEMATOPOIESIS AND STEM CELLS
Redundant mechanisms driven independently by RUNX1 and GATA2 for hematopoietic development
Erica Bresciani,Blake Carrington,Kai Yu,Erika M. Kim,Tao Zhen,Victoria Sanchez Guzman,Elizabeth Broadbridge,Kevin Bishop,Martha Kirby,Ursula Harper,Stephen Wincovitch,Stefania Dell’Orso,Vittorio Sartorelli,Raman Sood,Paul Liu
IMMUNOBIOLOGY AND IMMUNOTHERAPY
An autologous culture model of nodal B-cell lymphoma identifies ex vivo determinants of response to bispecific antibodies
Tobias Roider,Berit J. Brinkmann,Vladislav Kim,Mareike Knoll,Carolin Kolb,Philipp M. Roessner,Marie Bordas,Peter Dreger,Carsten Müller-Tidow,Wolfgang Huber,Martina Seiffert,Sascha Dietrich
Human iPSC-derived macrophages for efficient Staphylococcus aureus clearance in a murine pulmonary infection model
Anna Rafiei Hashtchin,Beate Fehlhaber,Miriam Hetzel,Felix Manstein,Jan Lennart Stalp,Silke Glage,Markus Abeln,Robert Zweigerdt,Antje Munder,Dorothee Viemann,Mania Ackermann,Nico Lachmann
Humoral immune reconstitution after anti-BCMA CAR T-cell therapy in relapsed/refractory multiple myeloma
Clinical Trials & Observations
Ying Wang,Chunrui Li,Jieyun Xia,Ping Li,Jiang Cao,Bin Pan,Xu Tan,Hujun Li,Kunming Qi,Xiangmin Wang,Ming Shi,Guangjun Jing,Zhiling Yan,Hai Cheng,Feng Zhu,Haiying Sun,Wei Sang,Depeng Li,Xi Zhang,Zhenyu Li,Junnian Zheng,Aibin Liang,Jianfeng Zhou,Kailin Xu
Infectious complications of CAR T-cell therapy across novel antigen targets in the first 30 days
Clinical Trials & Observations
Lekha Mikkilineni,Bonnie Yates,Seth M. Steinberg,Shilpa A. Shahani,John C. Molina,Tara Palmore,Daniel W. Lee,Rosandra N. Kaplan,Crystal L. Mackall,Terry J. Fry,Juan Gea-Banacloche,Theresa Jerussi,Veronique Nussenblatt,James N. Kochenderfer,Nirali N. Shah
LYMPHOID NEOPLASIA
Randomized phase 3 ALCANZA study of brentuximab vedotin vs physician’s choice in cutaneous T-cell lymphoma: final data
Clinical Trials & Observations
Steven M. Horwitz,Julia J. Scarisbrick,Reinhard Dummer,Sean Whittaker,Madeleine Duvic,Youn H. Kim,Pietro Quaglino,Pier Luigi Zinzani,Oliver Bechter,Herbert Eradat,Lauren Pinter-Brown,Oleg E. Akilov,Larisa Geskin,Jose A. Sanches,Pablo L. Ortiz-Romero,Michael Weichenthal,David C. Fisher,Jan Walewski,Judith Trotman,Kerry Taylor,Stephane Dalle,Rudolf Stadler,Julie Lisano,Veronica Bunn,Meredith Little,H. Miles Prince
ALL blasts drive primary mesenchymal stromal cells to increase asparagine availability during asparaginase treatment
Martina Chiu,Giuseppe Taurino,Erica Dander,Donatella Bardelli,Alessandra Fallati,Roberta Andreoli,Massimiliano G. Bianchi,Cecilia Carubbi,Giulia Pozzi,Laura Galuppo,Prisco Mirandola,Carmelo Rizzari,Saverio Tardito,Andrea Biondi,Giovanna D’Amico,Ovidio Bussolati
Early relapse identifies MCL patients with inferior survival after intensive or less intensive frontline therapy
Clinical Trials & Observations
David A. Bond,Jeffrey M. Switchenko,Diego Villa,Kami Maddocks,Michael Churnetski,Alina S. Gerrie,Subir Goyal,Krithika Shanmugasundaram,Oscar Calzada,Bhaskar Kolla,Veronika Bachanova,James N. Gerson,Stefan K. Barta,Brian T. Hill,Yazeed Sawalha,Peter Martin,Edward Maldonado,Max Gordon,Alexey V. Danilov,Natalie S. Grover,Stephanie Mathews,Madelyn Burkart,Reem Karmali,Nilanjan Ghosh,Steven I. Park,Narendranath Epperla,Talha Badar,Jin Guo,Mehdi Hamadani,Timothy S. Fenske,Mary-Kate Malecek,Brad S. Kahl,Christopher R. Flowers,Kristie A. Blum,Jonathon B. Cohen
Distinct clinical characteristics of DUX4- and PAX5-altered childhood B-lymphoblastic leukemia
Zhenhua Li,Shawn Hsien Ren Lee,Winnie Hui Ni Chin,Yi Lu,Nan Jiang,Evelyn Huizi Lim,Elaine Coustan-Smith,Kean Hui Chiew,Bernice Ling Zhi Oh,Grace Shimin Koh,Zhiwei Chen,Shirley Kow Yin Kham,Thuan Chong Quah,Hai Peng Lin,Ah Moy Tan,Hany Ariffin,Jun J. Yang,Allen Eng-Juh Yeoh
Frequent mutations of FBXO11 highlight BCL6 as a therapeutic target in Burkitt lymphoma
Chiara Pighi,Taek-Chin Cheong,Mara Compagno,Enrico Patrucco,Maddalena Arigoni,Martina Olivero,Qi Wang,Cristina López,Stephan H. Bernhart,Bruno M. Grande,Teresa Poggio,Fernanda Langellotto,Lisa Bonello,Riccardo Dall’Olio,Sandra Martínez-Martín,Luca Molinaro,Paola Francia di Celle,Jonathan R. Whitfield,Laura Soucek,Claudia Voena,Raffaele A. Calogero,Ryan D. Morin,Louis M. Staudt,Reiner Siebert,Alberto Zamò,Roberto Chiarle
A novel 3D culture model recapitulates primary FL B-cell features and promotes their survival
Claire Lamaison,Simon Latour,Nelson Hélaine,Valérie Le Morvan,Julien Saint-Vanne,Isabelle Mahouche,Céline Monvoisin,Christelle Dussert,Laëtitia Andrique,Laurent Deleurme,Elise Dessauge,Céline Pangault,Sylvain Baulande,Patricia Legoix,Marine Seffals,Léa Broca-Brisson,Kévin Alessandri,Martina Carlotti,Pierre Soubeyran,Jean-Philippe Merlio,Frédéric Mourcin,Pierre Nassoy,Gaëlle Recher,Karin Tarte,Laurence Bresson-Bepoldin
NUDT15 variants confer high incidence of second malignancies in children with acute lymphoblastic leukemia
Clinical Trials & Observations
Masanori Yoshida,Kazuhiko Nakabayashi,Wentao Yang,Aiko Sato-Otsubo,Shin-ichi Tsujimoto,Hiroko Ogata-Kawata,Tomoko Kawai,Keisuke Ishiwata,Mika Sakamoto,Kohji Okamura,Kaoru Yoshida,Ryota Shirai,Tomoo Osumi,Takaya Moriyama,Rina Nishii,Hiroyuki Takahashi,Chikako Kiyotani,Yoko Shioda,Keita Terashima,Sae Ishimaru,Yuki Yuza,Masatoshi Takagi,Yuki Arakawa,Akitoshi Kinoshita,Moeko Hino,Toshihiko Imamura,Daisuke Hasegawa,Yozo Nakazawa,Mayuko Okuya,Harumi Kakuda,Nao Takasugi,Akiko Inoue,Kentaro Ohki,Takako Yoshioka,Shuichi Ito,Daisuke Tomizawa,Katsuyoshi Koh,Kimikazu Matsumoto,Masashi Sanada,Nobutaka Kiyokawa,Akira Ohara,Seishi Ogawa,Atsushi Manabe,Akira Niwa,Kenichiro Hata,Jun J. Yang,Motohiro Kato
MYELOID NEOPLASIA
Engraftment characterization of risk-stratified AML in NSGS mice
Rafael Díaz de la Guardia,Talía Velasco-Hernandez,Francisco Gutiérrez-Agüera,Heleia Roca-Ho,Oscar Molina,Cesar Nombela-Arrieta,Alex Bataller,Jose Luis Fuster,Eduardo Anguita,Susana Vives,Lurdes Zamora,Josep Nomdedeu,María Teresa Gómez-Casares,Manuel Ramírez-Orellana,Helene Lapillonne,Verónica Ramos-Mejia,Juan Carlos Rodríguez-Manzaneque,Clara Bueno,Belen Lopez-Millan,Pablo Menéndez
Defining the transcriptional control of pediatric AML highlights RARA as a superenhancer-regulated druggable dependency
Monika W. Perez,Oscar Sias-Garcia,Alfred Daramola,Helen Wei,Maci Terrell,Raushan Rashid,Woojun D. Park,Kevin Duong,Terzah M. Horton,Feng Li,Nikitha Cherayil,Jost Vrabic Koren,Vincent U. Gant,Jacob J. Junco,Choladda V. Curry,Alexandra M. Stevens,Charles Y. Lin,Joanna S. Yi
Association of race and ethnicity with clinical phenotype, genetics, and survival in pediatric acute myeloid leukemia
Clinical Trials & Observations
PD-1 inhibition in advanced myeloproliferative neoplasms
Gabriela Hobbs,Cansu Cimen Bozkus,Erin Moshier,Mikaela Dougherty,Michal Bar-Natan,Lonette Sandy,Kathryn Johnson,Julia Elise Foster,Tina Som,Molly Macrae,Hetal Marble,Mohamed Salama,Siraj M. El Jamal,Nicole Zubizarreta,Martha Wadleigh,Richard Stone,Nina Bhardwaj,Camelia Iancu-Rubin,John Mascarenhas
ALCAM-EGFR interaction regulates myelomagenesis
Hongmei Luo,Dan Zhang,Fangfang Wang,Qiang Wang,Yu Wu,Maling Gou,Yiguo Hu,Wenyan Zhang,Jingcao Huang,Yuping Gong,Ling Pan,Tianshu Li,Pan Zhao,Danfeng Zhang,Ying Qu,Zhigang Liu,Tao Jiang,Yang Dai,Tingting Guo,Jiang Zhu,Lingqun Ye,Li Zhang,Weiping Liu,Qing Yi,Yuhuan Zheng
PLATELETS AND THROMBOPOIESIS
Ablation of collagen VI leads to the release of platelets with altered function
Vittorio Abbonante,Cristian Gruppi,Monica Battiston,Alessandra Zulian,Christian Andrea Di Buduo,Martina Chrisam,Lucia Sereni,Pierre-Alexandre Laurent,Claudio Semplicini,Elisabetta Lombardi,Mario Mazzucato,Francesco Moccia,Valeria Petronilli,Anna Villa,Luca Bello,Elena Pegoraro,Paolo Bernardi,Paola Braghetta,Luigi De Marco,Paolo Bonaldo,Alessandra Balduini
RED CELLS, IRON, AND ERYTHROPOIESIS
Restriction of HIV-1 infection in sickle cell trait
Namita Kumari,Mehdi Nouraie,Asrar Ahmad,Hatajai Lassiter,Javed Khan,Sharmin Diaz,Nowah Afangbedji,Songping Wang,Patricia E. Houston,Tatiana Ammosova,Miguel de Mulder Rougvie,Sohail Rana,Douglas F. Nixon,Kathryn Anastos,Jason Lazar,Audrey L. French,Stephen Gange,Adaora A. Adimora,M. Neale Weitzmann,Margaret Fischl,Mirjam-Colette Kempf,Seble Kassaye,James G. Taylor, VI,Sergei Nekhai
THROMBOSIS AND HEMOSTASIS
TRANSPLANTATION
Predicting mortality from intracranial hemorrhage in patients who undergo allogeneic hematopoietic stem cell transplantation
Clinical Trials & Observations
Xiying Ren,Qiusha Huang,Qingyuan Qu,Xuan Cai,Haixia Fu,Xiaodong Mo,Yu Wang,Yawei Zheng,Erlie Jiang,Yishan Ye,Yi Luo,Shaozhen Chen,Ting Yang,Yuanyuan Zhang,Wei Han,Feifei Tang,Wenjian Mo,Shunqing Wang,Fei Li,Daihong Liu,Xiaoying Zhang,Yicheng Zhang,Shuqing Feng,Feng Gao,Hailong Yuan,Dao Wang,Dingming Wan,Huan Chen,Yao Chen,Jingzhi Wang,Yuhong Chen,Ying Wang,Kailin Xu,Tao Lang,Xiaomin Wang,Hongbin Meng,Limin Li,Zhiguo Wang,Yanling Fan,Yingjun Chang,Lanping Xu,Xiaojun Huang,Xiaohui Zhang
Impact of cryopreservation and transit times of allogeneic grafts on hematopoietic and immune reconstitution
Clinical Trials & Observations
Katie Maurer,Haesook T. Kim,Thomas M. Kuczmarski,Heather M. Garrity,Augustine Weber,Carol G. Reynolds,Deborah Liney,Corey Cutler,Joseph H. Antin,John Koreth,Jerome Ritz,Roman M. Shapiro,Rizwan Romee,Catherine J. Wu,Robert J. Soiffer,Sarah Nikiforow,Vincent T. Ho,Mahasweta Gooptu
Anti-CD25 radioimmunotherapy with BEAM autologous hematopoietic cell transplantation conditioning in Hodgkin lymphoma
Clinical Trials & Observations
Alex F. Herrera,Joycelynne Palmer,Vikram Adhikarla,Dave Yamauchi,Erasmus K. Poku,James Bading,Paul Yazaki,Savita Dandapani,Matthew Mei,Robert Chen,Thai Cao,Nicole Karras,Pamela McTague,Auayporn Nademanee,Leslie Popplewell,Firoozeh Sahebi,John E. Shively,Jennifer Simpson,D. Lynne Smith,Joo Song,Ricardo Spielberger,Ni-Chun Tsai,Sandra H. Thomas,Stephen J. Forman,David Colcher,Anna M. Wu,Jeffrey Wong,Eileen Smith
VASCULAR BIOLOGY
RESEARCH LETTER
In a multi-institutional cohort of myeloid sarcomas, NFE2 mutation prevalence is lower than previously reported
Tauangtham Anekpuritanang,Matthew M. Klairmont,Joel Gradowski,Kohei Hagiwara,Nathanael G. Bailey,Pranil Chandra,Yiwei Liu,Heather L. Mulder,John Easton,Jinghui Zhang,Michael G. Martin,Anna B. Owczarczyk,Jennifer B. Dunlap,Guang Fan,Richard D. Press,Philipp W. Raess
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