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Gene Therapy
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Journal Articles
Brief Report
Byung-Chul Lee, Yifan Zhou, Erica Bresciani, Neval Ozkaya, Alina Dulau-Florea, Blake Carrington, Tae-Hoon Shin, Valentina Baena, Zulfeqhar A. Syed, So Gun Hong, Tao Zhen, Katherine R. Calvo, Paul Liu, Cynthia E. Dunbar
Journal:
Blood
Blood (2023) 141 (3): 231–237.
Published: 2023
Includes: Supplemental data
Journal Articles
P. Batty, A. M. Mo, D. Hurlbut, J. Ishida, B. Yates, C. Brown, L. Harpell, C. Hough, A. Pender, E. K. Rimmer, S. Sardo Infirri, A. Winterborn, S. Fong, D. Lillicrap
Journal:
Blood
Blood (2022) 140 (25): 2672–2683.
Published: 2022
Includes: Supplemental data
Journal Articles
Clinical Trials & Observations
Swetha Kambhampati, Monica Saumoy, Yecheskel Schneider, Stacy Pak, Lihua Elizabeth Budde, Matthew G. Mei, Tanya Siddiqi, Leslie L. Popplewell, Yi-Ping Wen, Jasmine Zain, Stephen J. Forman, Larry W. Kwak, Steven T. Rosen, Alexey V. Danilov, Alex F. Herrera, Nikhil R. Thiruvengadam
Journal:
Blood
Blood (2022) 140 (25): 2697–2708.
Published: 2022
Includes: Supplemental data
Journal Articles
Giulia Hardouin, Panagiotis Antoniou, Pierre Martinucci, Tristan Felix, Sandra Manceau, Laure Joseph, Cécile Masson, Samantha Scaramuzza, Giuliana Ferrari, Marina Cavazzana, Annarita Miccio
Journal:
Blood
Blood blood.2022016629.
Published: 2022
Includes: Supplemental data
Journal Articles
Alec B. Wilkens, Elena C. Fulton, Margot J. Pont, Gabriel O. Cole, Isabel Leung, Sylvia M. Stull, Matthew R. Hart, Irwin D. Bernstein, Scott N. Furlan, Stanley R. Riddell
Journal:
Blood
Blood (2022) 140 (21): 2261–2275.
Published: 2022
Includes: Supplemental data
Journal Articles
Jianqiong Zhu, Hongzhen Li, Wulin Aerbajinai, Chutima Kumkhaek, Mehdi Pirooznia, Ankit Saxena, Pradeep Dagur, Kyung Chin, Griffin P. Rodgers
Journal:
Blood
Blood (2022) 140 (21): 2276–2289.
Published: 2022
Includes: Supplemental data
Journal Articles
Ryan L Wong, Sarah Sackey, Devin Brown, Shantha Senadheera, Katelyn Masiuk, Jason P Quintos, Nicole Colindres, Luke Riggan, Richard A Morgan, Harry L Malech, Roger P Hollis, Donald B Kohn
Journal:
Blood
Blood blood.2022016074.
Published: 2022
Includes: Supplemental data
Journal Articles
Journal Articles
Clinical Trials & Observations
Paola Ghione, M. Lia Palomba, Anik R. Patel, Sabela Bobillo, Kevin Deighton, Caron A. Jacobson, Myrna Nahas, Anthony J. Hatswell, A. Scott Jung, Steve Kanters, Julia Thornton Snider, Sattva S. Neelapu, Maria Teresa Ribeiro, M. Alan Brookhart, Herve Ghesquieres, John Radford, John G. Gribben
Journal:
Blood
Blood (2022) 140 (8): 851–860.
Published: 2022
Includes: Supplemental data
Journal Articles
CME
Clinical Trials & Observations
Geoffrey D. E. Cuvelier, Brent R. Logan, Susan E. Prockop, Rebecca H. Buckley, Caroline Y. Kuo, Linda M. Griffith, Xuerong Liu, Alison Yip, Michael S. Hershfield, Paul G. Ayoub, Theodore B. Moore, Morna J. Dorsey, Richard J. O’Reilly, Neena Kapoor, Sung-Yun Pai, Malika Kapadia, Christen L. Ebens, Lisa R. Forbes Satter, Lauri M. Burroughs, Aleksandra Petrovic, Deepak Chellapandian, Jennifer Heimall, David C. Shyr, Ahmad Rayes, Jeffrey J. Bednarski, Sharat Chandra, Shanmuganathan Chandrakasan, Alfred P. Gillio, Lisa Madden, Troy C. Quigg, Emi H. Caywood, Blachy J. Dávila Saldaña, Kenneth DeSantes, Hesham Eissa, Frederick D. Goldman, Jacob Rozmus, Ami J. Shah, Mark T. Vander Lugt, Monica S. Thakar, Roberta E. Parrott, Caridad Martinez, Jennifer W. Leiding, Troy R. Torgerson, Michael A. Pulsipher, Luigi D. Notarangelo, Morton J. Cowan, Christopher C. Dvorak, Elie Haddad, Jennifer M. Puck, Donald B. Kohn
Journal:
Blood
Blood (2022) 140 (7): 685–705.
Published: 2022
Includes: Supplemental data
Journal Articles
Clinical Trials & Observations
Haneen Shalabi, Haiying Qin, Angela Su, Bonnie Yates, Pamela L. Wolters, Seth M. Steinberg, John A. Ligon, Sara Silbert, Kniya DéDé, Mehdi Benzaoui, Sophia Goldberg, Sooraj Achar, Dina Schneider, Shilpa A. Shahani, Lauren Little, Toni Foley, John C. Molina, Sandhya Panch, Crystal L. Mackall, Daniel W. Lee, Christopher D. Chien, Marie Pouzolles, Mark Ahlman, Constance M. Yuan, Hao-Wei Wang, Yanyu Wang, Jon Inglefield, Mary Anne Toledo-Tamula, Staci Martin, Steven L. Highfill, Gregoire Altan-Bonnet, David Stroncek, Terry J. Fry, Naomi Taylor, Nirali N. Shah
Journal:
Blood
Blood (2022) 140 (5): 451–463.
Published: 2022
Includes: Supplemental data
Journal Articles
Toshiaki Yoshikawa, Zhiwen Wu, Satoshi Inoue, Hitomi Kasuya, Hirokazu Matsushita, Yusuke Takahashi, Hiroaki Kuroda, Waki Hosoda, Shiro Suzuki, Yuki Kagoya
Journal:
Blood
Blood (2022) 139 (14): 2156–2172.
Published: 2022
Includes: Supplemental data
Journal Articles
Sarah K. Topfer, Ruopeng Feng, Peng Huang, Lana C. Ly, Gabriella E. Martyn, Gerd A. Blobel, Mitchell J. Weiss, Kate G. R. Quinlan, Merlin Crossley
Journal:
Blood
Blood (2022) 139 (14): 2107–2118.
Published: 2022
Includes: Supplemental data
Journal Articles
Lih Jiin Juang, Woosuk S. Hur, Lakmali M. Silva, Amy W. Strilchuk, Brenton Francisco, Jerry Leung, Madelaine K. Robertson, Dafna J. Groeneveld, Bridget La Prairie, Elizabeth M. Chun, Andrew P. Cap, James P. Luyendyk, Joseph S. Palumbo, Pieter R. Cullis, Thomas H. Bugge, Matthew J. Flick, Christian J. Kastrup
Journal:
Blood
Blood (2022) 139 (9): 1302–1311.
Published: 2022
Journal Articles
Julie Brault, Taylor Liu, Ezekiel Bello, Siyuan Liu, Colin L. Sweeney, Ronald J. Meis, Sherry Koontz, Cristina Corsino, Uimook Choi, Guillaume Vayssiere, Marita Bosticardo, Kennichi Dowdell, Cicera R. Lazzarotto, Aaron B. Clark, Luigi D. Notarangelo, Juan C. Ravell, Michael J. Lenardo, Benjamin P. Kleinstiver, Shengdar Q. Tsai, Xiaolin Wu, Gary A. Dahl, Harry L. Malech, Suk See De Ravin
Journal:
Blood
Blood (2021) 138 (26): 2768–2780.
Published: 2021
Includes: Supplemental data
Journal Articles
Nancy S. Bolous, Yichen Chen, Huiqi Wang, Andrew M. Davidoff, Meenakshi Devidas, Timothy W. Jacobs, Michael M. Meagher, Amit C. Nathwani, Ellis J. Neufeld, Bryan A. Piras, Carlos Rodriguez-Galindo, Ulrike M. Reiss, Nickhill Bhakta
Journal:
Blood
Blood (2021) 138 (18): 1677–1690.
Published: 2021
Includes: Supplemental data
Journal Articles
Nikoletta Psatha, Aphrodite Georgakopoulou, Chang Li, Vivek Nandakumar, Grigorios Georgolopoulos, Reyes Acosta, Kiriaki Paschoudi, Jemma Nelson, Daniel Chee, Anastasia Athanasiadou, Anastasia Kouvatsi, Alister Peter William Funnell, André Lieber, Evangelia Yannaki, Thalia Papayannopoulou
Journal:
Blood
Blood (2021) 138 (17): 1540–1553.
Published: 2021
Includes: Supplemental data
Journal Articles
Clinical Trials & Observations
David C. Bishop, Leighton E. Clancy, Renee Simms, Jane Burgess, Geetha Mathew, Leili Moezzi, Janine A. Street, Gaurav Sutrave, Elissa Atkins, Helen M. McGuire, Brian S. Gloss, Koon Lee, Wei Jiang, Karen Maddock, Georgia McCaughan, Selmir Avdic, Vicki Antonenas, Tracey A. O’Brien, Peter J. Shaw, David O. Irving, David J. Gottlieb, Emily Blyth, Kenneth P. Micklethwaite
Journal:
Blood
Blood (2021) 138 (16): 1504–1509.
Published: 2021
Includes: Supplemental data
Journal Articles
Journal Articles
Clinical Trials & Observations
Bryanna Reinhardt, Omar Habib, Kit L. Shaw, Elizabeth Garabedian, Denise A. Carbonaro-Sarracino, Dayna Terrazas, Beatriz Campo Fernandez, Satiro De Oliveira, Theodore B. Moore, Alan K. Ikeda, Barbara C. Engel, Gregory M. Podsakoff, Roger P. Hollis, Augustine Fernandes, Connie Jackson, Sally Shupien, Suparna Mishra, Alejandra Davila, Jack Mottahedeh, Andrej Vitomirov, Wenzhao Meng, Aaron M. Rosenfeld, Aoife M. Roche, Pascha Hokama, Shantan Reddy, John Everett, Xiaoyan Wang, Eline T. Luning Prak, Kenneth Cornetta, Michael S. Hershfield, Robert Sokolic, Suk See De Ravin, Harry L. Malech, Frederic D. Bushman, Fabio Candotti, Donald B. Kohn
Journal:
Blood
Blood (2021) 138 (15): 1304–1316.
Published: 2021
Includes: Supplemental data