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glycogen storage disease type iv
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Journal Articles
Caspar Da Cunha-Bang, MD PhD, Rudy Agius, Arnon P. Kater, Mark-David Levin, MD PhD, Anders Österborg, MD PhD, Mattias Mattsson, MD, Carsten Utoft Niemann, MD PhD
Journal:
Blood
Blood (2019) 134 (Supplement_1): 4304.
Published: 2019
Journal Articles
Pia Rude Nielsen, MD, Jens Ole Eriksen, MSc, PhD, Lise M. Lindahl, MD PhD, Ulrike Wehkamp, MD, Gitte Rinds Andersen, MSc, PhD, Michael Bzorek, Kirsten Grønbæk, Professor, MD DMSc, Niels Odum, MD DMSci, Thomas Litman, Prof., Lise Mette Rahbek Gjerdrum, MD PhD
Journal:
Blood
Blood (2019) 134 (Supplement_1): 2772.
Published: 2019
Journal Articles
Journal Articles
Courtney L Andersen, PhD, Amanda L Christie, MS, Alan Rosen, MS, Kim Maratea, DVM, PhD, Maureen Hattersley, Jon Travers, PhD, Justin Cidado, PhD, Sai Pulukuri, PhD, Jamal Saeh, PhD, Edwin Clark, PhD, Corinne Reimer, PhD, Jerome Mettetal, PhD
Journal:
Blood
Blood (2019) 134 (Supplement_1): 1273.
Published: 2019
Journal Articles
Kyle R Crassini, MBBS,BE,BSc, Eva Zhang, MBBS, Shalini Balendran, MBBS, Jane Freeman, BA,FRACP,FRCPA,MBBS,MPhil,MSc, Oliver Giles Best, PhDBSc, Cecily Forsyth, FRACP, FRCPA, MBBS, Naomi Mackinlay, Ping Han, MDPhD, William S. Stevenson, MBBS,PhD, Stephen Mulligan, PhDFRACP,FRCPA,MBBS
Journal:
Blood
Blood (2017) 130 (Supplement 1): 5321.
Published: 2017
Journal Articles
Hermann Eichler, MD, Pantep Angchaisuksiri, MD, Kaan Kavakli, MD, Paul Knöbl, MD PhD, Jerzy Windyga, Victor Jimenez-Yuste, Ute Friedrich, PhD, Philip Delff Andersen, Pratima Chowdary
Journal:
Blood
Blood (2017) 130 (Supplement 1): 3672.
Published: 2017
Journal Articles
Yutaka Niihara, MD, Rafael Razon, MD, Suvankar Majumdar, MD, Brian Claggett, PhD, Onyinye C. Onyekwere, MD, Alan Ikeda, MD, Tammuella Singleton, MD, Andrew Kohei Wood, MS, Rajani Singh, BS, Lan Tran, MPH, Charles William Stark, PharmD
Journal:
Blood
Blood (2017) 130 (Supplement 1): 685.
Published: 2017
Journal Articles
Emelie Curovic Curovic Rotbain, MD, Caspar Da Cunha-Bang, MD PhD, Henrik Hjalgrim, Klaus Rostgaard, MSc., Michael A Andersen, MD, Carsten Utoft Niemann, MD PhD, Henrik Frederiksen, associate professor, consultant, PhD
Journal:
Blood
Blood (2017) 130 (Supplement 1): 1742.
Published: 2017
Journal Articles
Barbara Gamberi, Miguel Hernandez, Christian Berthou, Eleni Tholouli, Elena Zamagni, Roman Hájek, Monique Minnema, Meletios A Dimopoulos, Jo Caers, Niels Frost Andersen, Bjorn Andreasson, Anders Waage, MD PhD, Gerard Crotty, Elisabeth Kueenburg, Barbara Rosettani, Antonia Di Micco, Pamela Bacon, Igor Blau
Journal:
Blood
Blood (2016) 128 (22): 3331.
Published: 2016
Journal Articles
Patricia A Merkel, Hannah E Giclas, Andrew Gibula, Gillian Andersen, Vijaya Knight, Jin-Sying Lin, Grace Castro, Jennifer Green, Adonis Stassinopoulos
Journal:
Blood
Blood (2016) 128 (22): 1455.
Published: 2016
Journal Articles
Khalid Aljamaan, MD, Talal Khalid Aljumah, MBBS, Saleh Aloraibi, PhD, Muhammad Absar, MSc PhD, Giuseppe Saglio, MD, Zafar Iqbal, MPhil PhD
Journal:
Blood
Blood (2015) 126 (23): 4987.
Published: 2015
Journal Articles
Christen Lykkegaard Andersen, MD, Volkert Siersma, MSc, Hans Carl Hasselbalch, MD PhD, Ole Weis Bjerrum, MD, Peter Felding, MD, Bent Lind, MD, Jan Palmblad, MD PhD, Niels de Fine Olivarius, MD
Journal:
Blood
Blood (2014) 124 (21): 2791.
Published: 2014
Journal Articles
Henrik Østergaard, PhD, Lene Hansen, Hermann Pelzer, PhD, Henrik Agersø, Anette A. Pedersen, Tina H. Glue, Laust B. Johnsen, PhD, Gorm Andersen, Jais R. Bjelke, Jens Breinholt, Henning Stennicke, MSc, PhD, Prafull S. Gandhi, PhD, Ole H. Olsen, PhD, Mette B. Hermit
Journal:
Blood
Blood (2014) 124 (21): 4233.
Published: 2014
Journal Articles
Paul E. R. Ellery, PhD, Cecilia Augustsson, PhD, Soren Andersen, PhD, Susan A. Maroney, DVM, PhD, Jeremy P Wood, PhD, Joan Cox Gill, MD, Ida Hilden, PhD, Alan E. Mast, MD PhD
Journal:
Blood
Blood (2014) 124 (21): 4241.
Published: 2014
Journal Articles
Christen Lykkegaard Andersen, MD, Volkert Siersma, MSc, Hanne Vestergaard, MD, Peter Felding, MD, Hans Carl Hasselbalch, MD, DMSc, Niels de Fine Olivarius, MD, Ole Weis Bjerrum, MD
Journal:
Blood
Blood (2013) 122 (21): 2831.
Published: 2013
Journal Articles
Eleshia Morrison, M.A., Joseph M Flynn, DO, MPH, Jeffrey A. Jones, MD, MPH, John C. Byrd, MD, Barbara L Andersen, PhD
Journal:
Blood
Blood (2012) 120 (21): 2075.
Published: 2012
Journal Articles
Nadia Rosencher, MD, Simon Frostick, MD, Martin Feuring, MD, Eva Kleine, Martina Brueckmann, MD, Andreas Clemens, MD, Charles Marc Samama, MD
Journal:
Blood
Blood (2012) 120 (21): 2269.
Published: 2012
Journal Articles
Marco Ladetto, MD, Simone Ferrero, Daniela Drandi, PhD, Federica Cavallo, Luigia Monitillo, Paola Ghione, Sara Barbiero, Mariella Grasso, Fausto Rossini, MD, Tommasina Guglielmelli, MD, Clotilde Cangialosi, MD, Anna Marina Liberati, MD, Vincenzo Callea, MD, Tommaso Caravita, MD, Luca De Rosa, MD, Francesco Pisani, Antonietta Pia Falcone, Patrizia Pregno, MD, Alberto Rocci, Roberto Passera, Mario Boccadoro, Antonio Palumbo, MD
Journal:
Blood
Blood (2011) 118 (21): 827.
Published: 2011
Journal Articles
Erich de Paula, Kaan Kavakli, Johnny Mahlangu, Yasmin Ayob, Steven R. Lentz, Massimo Morfini, László Nemes, Silva Zupancic Salek, Midori Shima, Jerzy Windyga, Silke Ehrenforth, Henning Friis Andersen, Ampaiwan Chuansumrit, and on behalf of 1804 (ADEPT-1) Investigators
Journal:
Blood
Blood (2010) 116 (21): 719.
Published: 2010
Journal Articles
Sabine Kayser, MD, Konstanze Döhner, MD, Jürgen Krauter, MD, Jochen Casper, MD, Heinz A. Horst, MD, PhD, Gerhard Held, MD, Sibylla Wilhelm, MD, Guido Kobbe, MD, Michael Lübbert, MD, Helmut R. Salih, MD, Katharina Götze, MD, Mathias J. Rummel, MD, PhD, Walter Fiedler, MD, Marie von Lilienfeld-Toal, MD, David Nachbaur, MD, Mohammed Wattad, MD, Daniela Späth, Patricia Erdmann, Arnold Ganser, MD, Hartmut Döhner, MD, Richard F. Schlenk, MD
Journal:
Blood
Blood (2010) 116 (21): 909.
Published: 2010
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